Currently Enrolling Studies 


ACHieve: A multi-center, longitudinal, observational study of children with achondroplasia


Omalizumab as Monotherapy and as Adjunct Therapy to Multi-Allergen OIT in Food Allergic Children and Adults (OUtMATCH)

Peanut Oral Immunotherapy Study 

Pediatric Peanut Allergy Oral Immunotherapy Study

Toddler Peanut Allergy Skin Patch Study 


Implementing a Guidelines-Based M-Health Intervention for High Risk Asthma Patients

Healthy Individuals or Type 2 Diabetes

Bioenergetics and Metabolism in Pediatric Patients

Immunometabolism in Pediatric Obesity


A Phase II, Open-label, Non-controlled, Intra-patient Dose-escalation Study to Characterize the Pharmacokinetics After Oral Administration of Eltrombopag in Pediatric Patients With Refractory, Relapsed or Treatment Naive Severe Aplastic Anemia or Recurrent Aplastic Anemia

Infection or Infectious Disease

A Phase 1, Single-Dose Safety and Pharmacokinetic Study of Oral and IV Tedizolid Phosphate (MK-1986) in Inpatients Under 2 Years Old

An Open label, Dose-finding, Pharmacokinetics, Safety, and Tolerability Study of Oritavancin Single Dose Infusion in Pediatric Subjects Less Than 18 Years of Age with Suspected or Confirmed Bacterial Infections (ORKIDS)

An Open-Label Study Of The Pharmacokinetics Of A Single Dose Of Telavancin In Pediatric Subjects Aged 1 To 17 Years

DMID 16-0095 CMV


A Multicenter, Randomized, Double-Blind, Placebo-Controlled, Crossover Study To Evaluate The Efficacy And Safety Of Zolmitriptan Nasal Spray For The Treatment Of Acute Migraine In Subjects Ages 6 To 11 Years, With An Open-Label Extension

Muscular Dystrophy

A Randomized, Double-Blind, Placebo-Controlled, Global Phase 3 Study of Edasalonexent in Pediatric Patients with Duchenne Muscular Dystrophy  


A Multi-center Phase III, Randomized, Open- Label Trial of Vigil (bi-shRNAfurin and GMCSF Augmented Autologous Tumor Cell Immunotherapy) in combination with Irinotecan and Temozolomide as a Second-Line Regimen for Ewing’s Sarcoma

A Phase 1, Open-Label, Multicenter, Dose Escalation Study of TB-403 in Pediatric Subjects with Relapsed or Refractory Medulloblastoma, Neuroblastoma, Ewing Sarcoma or Alveolar Rhabdomyosarcoma

A Phase I/II Study of Neratininb in children and Pediatric Patients with Relapsed or Refractory Solid Tumors or Hematologic Malignancies(POE16-01)

A Two-Part Study of TB-403 in Pediatric Subjects With Relapsed or Refractory Medulloblastoma

An Open-Label Study of Brentuximab Vedotin + Adriamycin, Vinblastine, and Dacarbazine in Pediatric Patients With Advanced Stage Newly Diagnosed Hodgkin Lymphoma

NMTRC 012 PEDS-PLAN – Pediatric Precision Laboratory Advanced Neuroblastoma Therapy

NMTRC 014 NMTT- Neuroblastoma Maintenance Therapy Trial Using Difluoromethylornithine (DFMO)

Phase I study of carfilzomib in combination with cyclophosphamide and etoposide for children with relapsed and refractory solid tumors and leukemias

Pregnant Women

The Expecting Study for Pregnant Women

Moon Study

Studies For Healthy Individuals

Brain Fuel

Happy Tummies Study

Nourish Study